Porphyria Targeting Therapies Market

Table Of Contents

1. BACKGROUND
1.1. Context
1.2. Project Report

2. EXECUTIVE SUMMARY

3. INTRODUCTION

4. MARKET LANDSCAPE
4.1. Market Landscape of Porphyria Drugs
4.2. Market Landscape of Porphyria Drug Developers

5. CASE STUDY
5.1 Case Study on Terminated and Dormant Programs

6. KEY MARKET INSIGHTS
6.1. Clinical Trial Analysis
6.2. KOL Analysis
6.3. Company Competitiveness Analysis
6.4. Publication Analysis
6.6 Partnership and Collaborations

7. COMPANY PROFILES
7.1. Agios Pharmaceuticals
7.2. Alnylam Pharmaceuticals
7.3. Clinuvel Pharmaceuticals
7.4. Mitsubishi Tanabe Pharma
7.5. Moderna Therapeutics
7.6. Palatin Technologies
7.7. Recordati Rare Diseases

8. MARKET FORECAST
8.1. Drugs Forecasted and Sales Estimated
8.1.1. GIVLAARI®
8.1.2. Panhematin™
8.1.3. SCENESSE®
8.1.4. MT-7117
8.1.5. Colestid
8.1.6. HARVONI®

8.2. Global Market Forecast, Till 2030
8.3. Distribution by Drug Class
8.4. Distribution by Type of Porphyria
8.5. Distribution by Route of Administration
8.6. Distribution by Region

9. APPENDICES
9.1. Clinical Trial Analysis
9.2. Publication Analysis
9.3. List of Figures
9.4. List of Companies and Organizations
9.2. Publication Analysis
9.3. List of Figures
9.4. List of Companies and Organizations

List Of Figures

Figure 1.1 Distribution by Phase of Development
Figure 1.2 Distribution by Drug Class
Figure 1.3 Distribution by Phase of Development and Drug Class
Figure 1.4 Distribution by Type of Porphyria
Figure 1.5 Distribution by Type of Porphyria and Phase of Development
Figure 1.6 Distribution by Route of Administration
Figure 1.7 Distribution by Mechanism of Action
Figure 1.8 Distribution by Drug Designation Obtained
Figure 1.9 Distribution by Type of Player and Ownership
Figure 1.10 Distribution by Company Size
Figure 1.11 Distribution by Year of Establishment
Figure 1.12 Players in North America
Figure 1.13 Players in Europe
Figure 1.14 Players in Rest of the World
Figure 1.15 Distribution by Phase of Development and Location of Headquarters
Figure 1.16 Distribution by Type of Molecule and Location of Headquarters
Figure 1.17 Distribution by Phase of Development and Type of Molecule
Figure 3.1 Distribution by Trial Registration Year
Figure 3.2 Distribution by Trial Phase
Figure 3.3 Distribution by Trial Status
Figure 3.4 Analysis by Type of Sponsor
Figure 3.5 Key Industry Players
Figure 3.6 Key Non-industry Players
Figure 3.7 Distribution by Type of Porphyria
Figure 3.8 Distribution by Type of Sponsor and Type of Porphyria
Figure 3.9 Distribution by Trial Status and Type of Porphyria
Figure 3.10 Distribution by Enrolled Patients, Trial Status and Geography
Figure 3.11 Distribution by Trial Status and Geography
Figure 3.12 Distribution of Number of Trials by Geography
Figure 4.1 Distribution by Type of Organization
Figure 4.2 Distribution by Region
Figure 4.3 Distribution by Qualification
Figure 4.4 Distribution by Principal Investigator and Type of Porphyria
Figure 4.5 Distribution by Type of Porphyria
Figure 4.6 KOL Activeness V/S Strength: Scatter Plot
Figure 4.7 Roots Analysis vs Third Party Score
Figure 4.8 Roots Analysis vs Third Party Score
Figure 4.9 Regional Distribution
Figure 4.10 Activeness of KOLs Investigating Drugs in Clinical Studies
Figure 5.1 Benchmarking of Prominent Companies
Figure 5.2 Distribution by Developers
Figure 6.1 Distribution by Year of Publication
Figure 6.2 Distribution by Type of Porphyria
Figure 6.3 Distribution by Type of Porphyria and Year of Publication
Figure 6.4 Key Journals based on Publications Count
Figure 6.5 Word Cloud: Emerging Focus Areas
Figure 6.6 Distribution by Most Popular Authors
Figure 7.1 Distribution by Year of Collaboration
Figure 7.2 Distribution by Type of Collaboration
Figure 7.3 Distribution by Year of Collaboration and Type of Collaboration
Figure 7.4 Distribution by Key Players
Figure 7.5 Key Drugs by Number of Partnerships
Figure 7.6 Intercontinental and Intracontinental Agreements
Figure 9.1 GIVLAARI®: Global Sales Forecast, 2021-2030
Figure 9.2 GIVLAARI®: Regional Sales Forecast, 2021-2030
Figure 9.3 Panhematin®: Global Sales Forecast, 2021-2030
Figure 9.4 Panhematin®: Regional Sales Forecast, 2021-2030
Figure 9.5 SCENESSE®: Global Sales Forecast, 2021-2030
Figure 9.6 SCENESSE®: Regional Sales Forecast, 2021-2030
Figure 9.7 MT-7117: Global Sales Forecast, 2022-20301
Figure 9.8 MT-7117: Regional Sales Forecast, 2022-20301
Figure 9.9 Colestid: Global Sales Forecast, 2022-2030
Figure 9.10 Colestid: Regional Sales Forecast, 2022-2030
Figure 9.11 HARVONI®: Global Sales Forecast, 2025-2030
Figure 9.12 HARVONI®: Regional Sales Forecast, 2025-2030
Figure 9.13 Distribution by Type of Porphyria, 2021
Figure 9.14 Distribution by Type of Porphyria, 2030
Figure 9.15 Acute Hepatic Porphyria: Global Sales Forecast, 2021-2030
Figure 9.16 Acute Hepatic Porphyria: Regional Sales Forecast, 2021-2030
Figure 9.17 AIP: Global Sales Forecast, 2021-2030
Figure 9.18 AIP: Regional Sales Forecast, 2021-2030
Figure 9.19 EPP: Global Sales Forecast, 2025-2030
Figure 9.20 EPP: Regional Sales Forecast, 2021-2030
Figure 9.21 HCP: Global Sales Forecast, 2027-2030
Figure 9.22 HCP: Regional Sales Forecast, 2027-2030
Figure 9.23 PCT: Global Sales Forecast, 2025-2030
Figure 9.24 PCT: Regional Sales Forecast, 2025-2030
Figure 9.25 Variegate Porphyria: Global Sales Forecast, 2027-2030
Figure 9.26 Variegate Porphyria: Regional Sales Forecast, 2027-2030
Figure 9.27 X-Linked Porphyria: Global Sales Forecast, 2024-2030
Figure 9.28 X-Linked Porphyria: Regional Sales Forecast, 2024-2030
Figure 9.29 Distribution by Route of Administration, 2021
Figure 9.30 Distribution by Route of Administration, 2030
Figure 9.31 Oral: Global Sales Forecast, 2022-2030
Figure 9.32 Oral: Regional Sales Forecast, 2022-2030
Figure 9.33 Intravenous: Global Sales Forecast, 2021-2030
Figure 9.34 Intravenous: Regional Sales Forecast, 2021-2030
Figure 9.35 Subcutaneous: Global Sales Forecast, 2021-2030
Figure 9.36 Subcutaneous: Regional Sales Forecast, 2021-2030
Figure 9.37 Overall Market Opportunity, 2021-2030
Figure 9.38 Distribution by Type of Drug Class, 2021, 2025 and 2030
Figure 9.39 Regional Distribution, 2021,2025 and 2030
Figure 9.40 Country-wise Distribution (Bubble Chart Representation)

List Of Companies

The following companies and organizations have been mentioned in the report. 

1. Access Biotechnology
2. Agios Pharmaceuticals
3. Alexion Pharmaceuticals
4. Alnylam Pharmaceuticals
5. Association pour la recherche en medecine interne (armi)
6. Atlas Molecular Pharma
7. Atlas Ventures
8. Atrium Health Wake Forest Baptist
9. Beam Therapeutics
10. Biotech Lab Singapore
11. Bioprofarma   Bago
12. Blackstone  
13. Brigham and Women's Hospital
14. Celnova Pharma
15. Chiesi Farmaceutici
16. Clinuvel   Pharmaceuticals
17. Committee for Medicinal Products of Human Use (CHMP)
18. Cycle Pharmaceuticals
19. Das Nationale Centrum für Tumorerkrankungen (NCT)
20. Digna Biotech
21. Disc Medicine
22. FARMOVS
23. Forge Biologics
24. Gilead Sciences
25. Hong Kong Winhealth Pharma Group
26. Hospital Universitario 12 de Octubre
27. Icahn School of Medicine
28. Ironwood Pharmaceuticals
29. Italchimici
30. Lundbeck
31. Medison Pharma
32. Mitsubishi Tanabe Pharma
33. Moderna Therapeutics
34. Mount Sinai Morningside
35. National Center for Research Resources (NCRR)
36. National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
37. National Institutes of Health (NIH)
38. NeuroDerm
39. Nordlandssykehuset 
40. Novartis
41. Novo Holdings
42. Office of Rare Diseases (ORD)
43. Palatin Technologies 
44. PANTHERx Rare
45. PAREXEL  
46. Recordati Rare Diseases
47. Roche
48. Strasbourg University Hospital
49. SurModics
50. Taiba 
51. The Royal Norwegian Ministry of Health
52. The University of Navarra
53. The University of Texas
54. The University of Texas Medical Branch
55. Therapeutic Goods Administration (TGA)
56. uniQure
57. University of Alabama
58. University of California
59. University of South Florida
60. University of Tromsø
61. University of Utah